-Hope For A Cure-
A concrete chance to save my sight and that of many other young children
My family, together with other families, are supporting researchers to find a cure to this rare disease.
They are committed to do everything they can to help to find a cure for us and for generations to come.
No child deserves a future in the dark.
Researchers need money to test possible treatments. Gene therapy is one of the possible options.
It has recently been used to effectively treat one variant of LCA (caused by gene RPE65) but more research is needed to apply gene therapy to the other forms of LCA including mine.
We are also looking into testing potential drugs to slow down the progression of the disease.
A cure is possible but It is important that we act fast. The world is slowly going dark for me and without this work the cure will arrive too late to save my vision.
More details on Treatments